A hemophilia study in the UK made headlines this week due to its “mind-blowing” results. BBC reports that the 13 person trial has given hope to these patients suffering from Hemophilia requiring daily factor VIII injections. They further state, “The virus is used like a postman to deliver the genetic instructions to the liver, which then starts producing factor VIII.”
From the article:
Prof John Pasi, who led the trials at Barts and Queen Mary University of London, said: “This is huge.
“It’s ground-breaking because the option to think about normalising levels in patients with severe haemophilia is absolutely mind-blowing.
“To offer people the potential of a normal life when they’ve had to inject themselves with factor VIII every other day to prevent bleeding is transformational.”